講演情報

[3P-930]Targeting the heart in DMD: DG9 peptide boosts PMO delivery and exon skipping to preserve cardiac function

○Rika Maruyama1, Md Nur Ahad Shah1, Harry Wilton-Clark1, Courtney S. Young2, Melissa J. Spencer2, Hong M. Moulton3, Gavin Y. Oudit4, Toshifumi Yokota1 (1. Dept. of Medical Genetics, University of Alberta, 2. Dept. of Neurology, University of California, Los Angeles, 3. Dept. of Biomedical Sciences, Oregon State University, 4. Mazankowski Alberta Heart Institute, University of Alberta)

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