Presentation Information

[O16-05]Two cases of SMA type 1 leading to tracheostomy after treatment of onasemnogen abeparvovec and risdiplam.

Maiko Nakashima1, Shotaro Kaku1,2, Noriko Udagawa1, Shuji Hashimoto1, Natsuko Arai1,3, Taichi Imaizumi1, Hisako Yamamoto1,4, Kenji Sugai1,3, Hitoshi Yamamoto1, Hirohumi Komaki4, Toshiyuki Iwasaki1, Yusaku Miyamoto1, Naoki Shimizu1 (1.Department of Pediatrics, St. Marianna University, Kanagawa, Japan, 2.Clinic WIZ Noborito Yuen Pediatrics, Kanagawa, Japan, 3.Department of Pediatrics, Soleil Kawasaki, a welfare and medical facility for severely ill children and persons, Kanagawa, Japan, 4.Department of Child Neurology, National center of neurology and psychiatry, Tokyo, Japan)

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