Presentation Information

[O25-02]Intracerebroventricular enzyme replacement and umbilical cord blood transplantation for mucopolysaccharidosis type II

Yuki Ueda1, Shinsuke Hirabayashi1, Satoshi Yamada1, Yasuyoshi Hiramatsu1, Sachiko Nakakubo1, Midori Nakajima1, Takeru Gotoh1, Jutaro Abe1, Yukayo Terashita1, Kiyoshi Egawa1, Atsushi Manabe1, Torayuki Okuyama2 (1.Department of Pediatrics, Hokkaido University Hospital, Sapporo, Japan, 2.Department of Genomic Medicine, Saitama Medical University)

Password required to view