Presentation Information

[P13-01]Treatment of spinal muscular atrophy treated with nusinersen at our hospital

Yuki Iai1, Shuichi Shimakawa1, Ryuichi Saura2, Kenji Kuroda2, Noriko Otsuki3, Kayoko Saito3, Hikaru Kitahara2, Akira Ashida1 (1.Osaka Medical and Pharmaceutical University of Pediatrics, Takatsuki, Japan, 2.Osaka Medical and Pharmaceutical University of Rehabilitation, Takatsuki, Japan, 3.Genomics, Tokyo Women's Medical University,Japan)

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