Presentation Information
[BO-4]Long-term efficacy of gene therapy for AADC deficiency and development of diagnostic system
○Marina Mizobe1, Karin Kojima1, Chika Watanabe1, Shin-ichi Muramatsu2, Hitoshi Osaka1, Takanori Yamagata1,3 (1.Department of Pediatrics, Jichi Medical University, Tochigi, Japan, 2.Division of Neurological Gene Therapy, Jichi Medical University, Tochigi, Japan, 3.Tochigi Rehabilitation Center, Tochigi, Japan)