Session Details

[S07]Symposium 7 Future Directions in Pediatrics: From Treatment to Prevention

Thu. Dec 18, 2025 3:55 PM - 5:55 PM JST
Thu. Dec 18, 2025 6:55 AM - 8:55 AM UTC
Room 3 (303, 3F, PACIFICO Yokohama)
Chairs:Atsuo Kikuchi(Department of Pediatrics, Tohoku University Graduate School of Medicine)/Toshiki Takenouchi(Department of Pediatric Neurology, Okayama University Graduate School of Medicine, Dentistry and Pharmaceutical Sciences)
[English Session]

[S7-1]Emerging Gene Therapies for DMD: Clinical Expectations and Ongoing Challenges

Hiroyuki Awano (Organization for Research Initiative and Promotion, Tottori University)

[S7-2]Advancing Therapeutics for Pediatric Liver Diseases: From PFIC2 Drug Development to the Research Platform CIRCLe

Hisamitsu Hayashi1,2 (1.Graduate School of Pharmaceutical Sciences, The University of Tokyo, Tokyo, Japan, 2.General Incorporated Association Delta Compass, Tokyo, Japan)

[S7-3]Proteomic Screening and Diagnosis of Inborn Errors of Immunity Using Dried Blood Spots: Toward Early Intervention

Kazushi Izawa (Department of Pediatrics, Kyoto University Graduate School of Medicine, Kyoto, Japan)

[S7-4]How can information from large‑scale cohort studies be applied to pediatric practice?

Emiko Noguchi1,2 (1.Department of Medical Genetics, Institute of Medicine, University of Tsukuba, 2.Japan Environment and Children's Study, National Institute for Environmental Studies)