Presentation Information

[AO-01-5]Allele selective silencing of polyQ proteins by SNA-modified siRNA targeting CAG expansions in mice

Kentaro Maeda1, Tomoki Hirunagi1, Kentaro Sahashi1, Madoka Iida1, Yukiko Kamiya2, Hiroyuki Asanuma3, Masahisa Katsuno1 (1.Department of Neurology, Nagoya University Graduate School of Medicine, Japan, 2.Laboratory of Bioanalytical Chemistry, Kobe Pharmaceutical University, Japan, 3.Department of Biomolecular Engineering, Nagoya University Graduate School of Engineering, Japan)

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