Presentation Information
[AO-02-1]A Phase 1 Study of NS-035 in Patients with Fukuyama Congenital Muscular Dystrophy
Go Fujino1, Asuka Kitamura1, Akiko Takahashi1, Meiko Maeda1, Akatsuki Kubota1, Yukino Tokuyama2, Ikue Wada2, Kazuhiro Kobayashi3, Hirofumi Komaki4, Mariko Taniguchi-Ikeda5, Keiko Ishigaki6, Tatsushi Toda1 (1.Department of Neurology, Graduate School of Medicine, The University of Tokyo, Japan, 2.Clinical Research Promotion Center, The University of Tokyo Hospital, Japan, 3.Division of Molecular Brain Science, Kobe University Graduate School of Medicine, Japan, 4.Department of Child Neurology, National Center Hospital, National Center of Neurology and Psychiatry, Japan, 5.Department of Clinical Genetics, Fujita Health University Hospital, Japan, 6.Department of Pediatrics, Tokyo Women's Medical University School of Medicine, Japan)