Presentation Information
[1S08m-4]C9orf72-Linked ALS: GEM Body Dysfunction and RNA Metabolism Disruption
*Hitomi Tsuiji1 (1. School of Pharmacy, Aichi Gakuin University, Nagoya, Japan)
Keywords:
amyotrophic lateral sclerosis,splicing,CRISPR/dCas13,phase separation
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