Session Details

[26F-pm]Genes and gene therapy of diseases

Sat. Mar 26, 2022 4:54 PM - 5:54 PM JST
Sat. Mar 26, 2022 7:54 AM - 8:54 AM UTC
[Room F] Exhibition Room 211 Bldg. 2: 1F
Chair: Hidetoshi Arima

[26F-pm18S]Gene therapy for galactosialidosis model mice using AAV5 carrying the human CTSA and modified NEU1 which does not cause intracellular crystallization.

○Mizuki Miyoshi1, Jun Tsukimoto1, Yuto Horii1, Yoshie Takeuchi2, Nijiho Kamori2, Rin Fukuike2, Kohji Itoh1,2 (1. Grad. Sch. Pharm. Sci, Tokushima Univ., 2. Facult. Pharm. Sci., Tokushima Univ.)

[26F-pm19S]Generation and in vivo application of adenovirus vectors carrying CRISPR-Cas12a system with improved nuclear localization

○Tomohito Tsukamoto1, Haruna Mizuta2, Eiko Sakai1, Fuminori Sakurai1,2, Hiroyuki Mizuguchi1,2,3,4,5 (1. Grad. Sch. Pharm. Sci., Osaka Univ., 2. Undergrad. Sch. Pharm. Sci., Osaka Univ., 3. Nat. Inst. Biomed. Innov. Health Nutr., 4. Ctr. Adv. Med. Engin. Inform., Osaka Univ., 5. OTRI, Osaka University)

[26F-pm20S]Evaluation of anti-fibrotic effects of oncolytic reovirus on fibrotic liver

○Ikuho Ishigami1, Shunsuke Inoue1, Yuki Kibe1, Shinichiro Nakamura3, Hiroyuki Mizuguchi1,2,4,5, Fuminori Sakurai1 (1. Grad. Sch. Pharm. Sci., Osaka Univ., 2. NIBIOHN, 3. Sch. Vet. Med., Azabu Univ., 4. MEI Cent., Osaka Univ, 5. OTRI, Osaka Univ)

[26F-pm21S]EphA2 Phosphorylation at Ser-897 and Abi1 expression are essential to the enhanced cell motility in BRAFV600E/PTEN-deficient cells

○Shutaro Nagai1, Yutaka Yasuta1, Yue Zhou1, Hiroaki Sakurai1, Satoru Yokoyama1 (1. Grad. Sch. Pham. Sci., Univ. Toyama)

[26F-pm22S]In vivo analysis of Maip1: a target gene of NAFLD/NASH-related miR-27b

○Yuka Masuda1, Eiko Sakai1, Marcos Taracena1, Fuminori Sakurai1, Hiroyuki Mizuguchi1,2,3,4 (1. Grad. Sch. Pharm. Sci., Osaka Univ., 2. Global Ctr. for Med. Eng. and Inf., Osaka Univ., 3. OTRI, Osaka Univ., 4. NIBIOHN)