Presentation Information
[3O18a-09(ST15-08)]In vivo efficacy and toxicity evaluation of 2-hydroxypropyl-β-cyclodextrin with high degree of substitution as potential therapeutic candidates for Niemann-Pick disease type C
○Mayuko Tanaka1, Yusei Yamada2, Toru Miwa3, Hiroki Takeda1, Yorihisa Orita1, Toru Takeo1, Naomi Nakagata1, Taishi Higashi1, Keiichi Motoyama1, Hidetoshi Arima4, Takahiro Seki5, Yuki Kurauchi1, Hiroshi Katsuki1, Muneaki Matsuo6, Yoichi Ishitsuka1 (1.Kumamoto Univ., 2.Miyazaki Univ. Hosp., 3.Teikyo University Mizoguchi Hosp., 4.Daiichi Pharmaceutical Univ., 5.Himeji Dokkyo Univ., 6.Saga Univ.)
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