Presentation Information

[1P-058]RNA hacking enables DDS-independent in vivo therapeutic efficacy in extrahepatic tissues

*Rena Nagata1, Tomoki Kida1, Miko Kato1, Takahiro Hiraide2, Yoji Hakamata3, Masahiko Fujisawa3, Toshihiro Ihara1, Masaharu Kataoka4, Shin-ichi Sato1,5, Yousuke Katsuda1,5,6 (1. Advanced Science and Engineering, Kumamoto University, 2. Department of Cardiology, Keio University School of Medicine, 3. Department of Veterinary Nursing and Technology, Faculty of Veterinary Medicine, Nippon Veterinary and Life Science University, 4. The Second Department of Internal Medicine, University of Occupational and Environmental Health, 5. StapleBio Inc., 6. Institute for Integrated Cell-Material Sciences (WPI-iCeMS), Kyoto University)

Keywords:

Nucleic acid therapeutics,Gene expression regulation,Chemical modification,DDS,in vivo