Presentation Information

[28-19-am12]First in human clinical study of ex vivo gene therapy using autologous adipocytes for familial LCAT deficiency syndrome

○Masayuki Kuroda1, Wada Jun2, Maezawa Yoshiro3, Kubota Yoshitaka3, Mitsukawa Nobuyuki3, Yamamoto Tokuo4, Aso Masayuki4, Hanaoka Hideki1, Saito Yasushi5, Yokote Koutaro5 (1. Chiba Univ. Hosp., Chia Univ., 2. Grad. Sch. Med., Okayama Univ., 3. Grad. Sch. Med., Chiba Univ., 4. CellGenTech, Inc., 5. Chiba Univ.)