講演情報
[_LB-5]Pentatricopeptide repeat protein targeting CUG repeat RNA ameliorates RNA toxicity in a myotonic dystrophy type 1 mouse model
Joe Nemoto1, Takayoshi Imai2, Maiko Miyai3, Yusuke Yagi2,4, Osamu Nakanishi2, Hideki Mochizuki3, Masayuki Nakamori1,3 (1.Department of Neurology, Graduate School of Medicine, Yamaguchi University, 2.EditForce, Inc, 3.Department of Neurology, Osaka University Graduate School of Medicine, 4.Faculty of Agriculture, Kyusyu University)